A one-time gene therapy using a patient’s own stem cells has effectively cured a deadly immune disorder in 95% of treated ...

For children born with severe combined immunodeficiency due to adenosine deaminase deficiency (ADA-SCID), an investigational ...

In a clinical trial led by University of Toronto researchers, an allogeneic stem cell–derived islet therapy (zimislecel) restored insulin production and ended severe hypoglycemia in adults with type 1 ...

Overall and event-free survival of 100 and 95%, respectively, seen with autologous CD34+ hematopoietic stem-cell lentiviral gene therapy.

A new therapy for type 1 diabetes could nix the need for insulin injections. Just a single infusion of lab-grown pancreatic cells let patients’ bodies make all the insulin they needed, scientists ...

New research found that gene therapy for children with a form of severe combined immunodeficiency was successful in 95% of ...