Find out if it’s time to ask about your child’s symptoms — and if they could be a sign of Duchenne. Duchenne muscular dystrophy — sometimes referred to simply as Duchenne — is a genetic disorder that ...

Still, CEO Doug Ingram claimed removing the two drugs, Vyondys 53 and Amondys 45, from market would make “little sense” and ...

While it’s established that Duchenne muscular dystrophy (DMD) causes a loss of muscle mass and strength, few studies have examined the gastrointestinal issues tied to DMD. Initial fractures are the ...

Capricor Therapeutics shares rose over 3% in after-hours trading after the company said during its third-quarter conference ...

Q3 2025 Management View Curran Simpson, President and CEO, highlighted strong momentum in late-stage gene therapy programs, ...

A long-running confirmatory trial of two of Sarepta Therapeutics’ Duchenne muscular dystrophy drugs has missed its main goal.

Susan and Chris Finazzo have enrolled their sons Dylan and Chase in a study of gene therapy for Duchenne muscular dystrophy. The experimental treatment is still being studied but researchers hope it ...

The primary endpoint and key secondary endpoints were met for the vamorolone 6mg/kg/day treatment group. The Food and Drug Administration (FDA) has approved Agamree ® (vamorolone) for the treatment of ...

DUBLIN--(BUSINESS WIRE)--The "Global Duchenne Muscular Dystrophy Market and Competitive Landscape - 2021" report has been added to ResearchAndMarkets.com's offering. Global Duchenne Muscular Dystrophy ...

On Saturday, November 22, those who head to The Grand Theater in Ellsworth will get a chance to see the state of Maine in a ...