TipRanks on MSN

Neurogene completes FDA discussion on Embolden trial, announces NGN-401 data

Neurogene (NGNE) announced the company has completed discussions with the FDA on its Embolden registrational trial protocol and plans to initiate ...
Natural Science News

Protein in mosquito antennae detects insecticide, triggering defense response

New research reveals mosquito proteins, Sensory Appendage Proteins (SAPs), help them find people & resist insecticides. These ...
TipRanks on MSN

Circio Unveils Breakthrough in Gene Therapy with AAV-circVec Technology

Targovax ASA ( ($GB:0RIS) ) has shared an announcement. Circio Holding ASA announced significant advancements in their AAV-circVec technology, ...

Form Bio and Cure Rare Disease Partner to Accelerate Genetic Medicine Development, Advancing CRD's Duchenne Muscular Dystrophy Program

Partnership leverages AI-powered genome design to optimize AAV constructs, accelerate lead candidate selection, and improve drug substance manufacturability for rare and ultra-rare neuromuscular ...
PharmiWeb

SonoThera™ Presents New Data at ESGCT 2025 Demonstrating Expression of Full-Length Human Dystrophin Using Targeted, Ultrasound-Mediated Delivery to Treat …

New data demonstrates the ability of UMD technology to deliver genetic medicines, allowing for full-length human dystrophin ...

Sarepta Therapeutics to Present New Data from its Neuromuscular Portfolio at 2025 World Muscle Society Congress

Sarepta Therapeutics, Inc. (NASDAQ:SRPT), the leader in precision genetic medicine for rare diseases, will present at the 30 th Annual Congress of the World Muscle Society (WMS) 2025 Congress, taking ...