The FDA has approved berotralstat oral pellets for prophylactic use in patients aged 2 to than 12 years with hereditary ...

Lizzy McMahon, 43, told Newsweek that their son is determined to help his dad remember their favorite phrases.

Each week, therapists from Kindering visit Yasmin Guzman's home in Bothell to work with her joyous 2-year-old, Emma.

Amber Freed tells PEOPLE how she worked for years to find a treatment for her son Maxwell's SLC6A1 diagnosis, and finally got the treatment administered in September, making history in the process.

Chalkbeat reports on delays in Philadelphia's early intervention services, hindering vulnerable kids' access to mandated ...

Harlow is defying the odds after receiving groundbreaking gene therapy for a rare brain disorder. Her progress has been called "a miracle" by her family ...

Stability has become ever scarcer in the lives of Milan’s parents since he arrived in November 2023. Milan needs multiple ...

White House may extend ACA (Obamacare) subsidies for two years Trump faces political balancing act on rising premiums Insurer shares jump on extension reports Nov 24 (Reuters) - The White House is ...

Oliver Chu faced a limited life when born with inherited condition Hunter syndrome, which causes progressive damage to the body and brain.

A three-year-old Oliver (Ollie) Chu has become the world’s first patient to receive a revolutionary stem cell gene therapy for Hunter syndrome. This rare, progressive, inherited disorder damages the ...

HINESVILLE, Ga. (WTOC) - A 2-year-old is dead in Hinesville. Hinesville police officers went to a home in the 600 block of Slade Street after receiving a report of a child with a gunshot wound. The ...

Oklahoma City police have arrested the parents of a 2-year-old toddler after she was mauled to death by a family pet earlier this week in northeast OKC. According to the Oklahoma City Police ...