Sarepta slumps as gene therapy setback adds to drug pipeline woes

Shares of Sarepta sank 36% before the bell on Tuesday after a trial for two gene-targeted therapies for a muscle-wasting ...

Five-year data of AGAMREE® (vamorolone) in patients with DMD show improved safety profile with comparable effectiveness to standard of care corticosteroids

Ad hoc announcement pursuant to Art. 53 LR Comparable long-term effectiveness to standard of care corticosteroids over 5 years Normal growth maintained, in contrast to growth suppression commonly seen ...

Sarepta’s stock plummets as disappointing trial data raise questions on DMD drug’s success

Shares of Sarepta Therapeutics Inc. plunged in extended trading Monday after the biotechnology company disclosed ...

Sarepta's Duchenne gene therapy misses main goal in late-stage study; shares fall

Sarepta said on Monday that its late-stage study testing two gene-targeted therapies for Duchenne muscular dystrophy did not ...

Sarepta's shares plunge after trial for muscle-wasting disease drugs miss key goal

Sarepta said on Monday that its late-stage study testing two gene-targeted therapies for Duchenne muscular dystrophy did not ...
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Sarepta Crashes After Two Muscular Dystrophy Drugs Fail Confirmatory Tests

Sarepta stock crashed late Monday after the biotech company said two of its muscular dystrophy drugs failed their ...

Solid Biosciences Reports Third Quarter 2025 Financial Results and Provides Update on INSPIRE DUCHENNE Clinical Trial Progress and Planned Regulatory Discussions

Duchenne (SGT-003): 23 participants have been dosed in the INSPIRE DUCHENNE trial as of October 31, 2025; Solid expects to ...

Sarepta plunges after late-stage Duchenne trial failure

Sarepta Therapeutics ( SRPT) shares fell after its late-stage trial for two gene therapies, AMONDYS 45 (casimersen) and VYONDYS 5 (golodirsen), aimed at treating Duchenne muscular dystrophy, did not ...

Capricor Therapeutics Publishes Peer-Reviewed Study in Biomedicines Describing the Mechanism of Action and Potency Assay for its Investigational Cell Therapy, Deramiocel

Publication highlights Deramiocel’s anti-fibrotic activity and describes a validated potency assay supporting quality control and product ...

Community comes together to help boy with Duchenne Muscular Dystrophy

A San Diego community upgraded an adaptive van for Eddie Garcia, a boy with Duchenne Muscular Dystrophy, providing a motorized ramp to ease his mobility challenges.

Nebraska football players and coaches fulfill dreams for Make-A-Wish teens

Ben Skinner and Jagger Casey spent the weekend living out their dream of being a Nebraska football player, leading the team ...